this post was submitted on 28 Apr 2024
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FDA approves Pfizer's first gene therapy for rare inherited bleeding disorder (www.nbcnews.com)
submitted 6 months ago by MicroWave@lemmy.world to c/health@lemmy.world
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The agency greenlit the drug, which will be marketed as Beqvez, for adults with moderate to severe hemophilia B who meet certain requirements.

The Food and Drug Administration on Friday approved Pfizer’s treatment for a rare genetic bleeding disorder, making it the company’s first-ever gene therapy to win clearance in the U.S. 

The agency greenlit the drug, which will be marketed as Beqvez, for adults with moderate to severe hemophilia B who meet certain requirements.

The treatment will be available by prescription to eligible patients this quarter, a Pfizer spokesperson told CNBC. It has a hefty $3.5 million price tag, before insurance and other rebates, the spokesperson added, making it by far one of the most expensive drugs in the U.S.

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[–] Valmond@lemmy.world 2 points 6 months ago

This is great, hear me out.

First stuff doesnt work well and are expensive.

Then they get normal, works better and are less expensive.

And in the end they work perfectly well and cost almost nothing.

Cellphones is a good example but there are loads of others. So yeah, it's expensive but will pave the way for cheap good treatment in the future.